| 88 Compassionate Allowance Conditions |
|
| 1. Acute Leukemia |
26. Krabbe Disease (KD) – Infantile |
| 2. Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
27. Large Intestine Cancer - with distant metastasis or inoperable, unresectable or recurrent |
| 3. Alexander Disease (ALX) – Neonatal and Infantile |
28 Lesch-Nyhan Syndrome (LNS) |
| 4. Amyotrophic Lateral Sclerosis (ALS) |
29. Liver Cancer |
| 5. Anaplastic Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
30. Mantle Cell Lymphoma (MCL) |
| 6. Astrocytoma - Grade III and IV |
31. Metachromatic Leukodystrophy (MLD) – Late Infantile |
| 7. Bladder Cancer - with distant metastases or inoperable or unresectable |
32. Niemann-Pick Disease (NPD) – Type A |
| 8. Bone Cancer - with distant metastases or inoperable or unresectable |
33. Non-Small Cell Lung Cancer - with metastases to or beyond the hilar nodes or inoperable, unresectable or recurrent |
| 9. Breast Cancer - with distant metastases or inoperable or unresectable |
34. Ornithine Transcarbamylase (OTC) Deficiency |
| 10. Canavan Disease (CD) |
35. Osteogenesis Imperfecta (OI) – Type II |
| 11. Cerebro Oculo Facio Skeletal (COFS) Syndrome |
36. Ovarian Cancer - with distant metastases or inoperable or unresectable |
| 12. Chronic Myelogenous Leukemia (CML) – Blast Phase |
37. Pancreatic Cancer |
| 13. Creutzfeldt-Jakob Disease (CJD) – Adult |
38. Peritoneal Mesothelioma |
| 14. Ependymoblastoma (Child Brain Tumor) |
39. Pleural Mesothelioma |
| 15. Esophageal Cancer |
40. Pompe Disease – Infantile |
| 16. Farber’s Disease (FD) – Infantile |
41. Rett Syndrome |
| 17. Friedreichs Ataxia (FRDA) |
42. Salivary Tumors |
| 1.8 Frontotemporal Dementia (FTD), Picks Disease -Type A – Adult |
43. Sandhoff Disease |
| 19. Gallbladder Cancer |
44. Small Cell Cancer (of the Large Intestine, Ovary, Prostate, or Uterus) |
| 20. Gaucher Disease (GD) – Type 2 |
45. Small Cell Lung Cancer |
| 21. Glioblastoma Multiforme (Brain Tumor) |
46. Small Intestine Cancer - with distant metastases or inoperable, unresectable or recurrent |
| 22. Head and Neck Cancers - with distant metastasis or inoperable or uresectable |
47. Spinal Muscular Atrophy (SMA) – Types 0 And 1 |
| 23. Infantile Neuroaxonal Dystrophy (INAD) |
48. Stomach Cancer - with distant metastases or inoperable, unresectable or recurrent |
| 24. Inflammatory Breast Cancer (IBC) |
49. Thyroid Cancer |
| 25. Kidney Cancer - inoperable or unresectable |
50. Ureter Cancer - with distant metastases or inoperable, unresectable or recurrent |
|
|
| New Conditions Added in 2010 |
|
| 1. Alstrom Syndrome |
20. Leigh’s Disease |
| 2. Amegakaryocytic Thrombocytopenia |
21. Maple Syrup Urine Disease |
| 3. Ataxia Spinocerebellar |
22. Merosin Deficient Congenital Muscular Dystrophy |
| 4. Ataxia Telangiectasia |
23. Mixed Dementia |
| 5. Batten Disease |
24. Mucosal Malignant Melanoma |
| 6. Bilateral Retinoblastoma |
25. Neonatal Adrenoleukodystrophy |
| 7. Cri du Chat Syndrome |
26. Neuronal Ceroid Lipofuscinoses, Infantile Type |
| 8. Degos Disease |
27. Niemann-Pick Type C |
| 9. Early-Onset Alzheimer’s Disease |
28. Patau Syndrome |
| 10. Edwards Syndrome |
29. Primary Progressive Aphasia |
| 11. Fibrodysplasia Ossificans Progressiva |
30. Progressive Multifocal Leukoencephalopathy |
| 12. Fukuyama Congenital Muscular Dystrophy |
31. Sanfilippo Syndrome |
| 13. Glutaric Acidemia Type II |
32. Subacute Sclerosis Panencephalitis |
| 14. Hemophagocytic Lymphohistiocytosis (HLH), Familial Type |
33. Tay Sachs Disease |
| 15. Hurler Syndrome, Type IH |
34. Thanatophoric Dysplasia, Type 1 |
| 16. Hunter Syndrome, Type II |
35. Ullrich Congenital Muscular Dystrophy |
| 17. Idiopathic Pulmonary Fibrosis |
36. Walker Warburg Syndrome |
| 18. Junctional Epidermolysis Bullosa, Lethal Type |
37. Wolman Disease |
| 19. Late Infantile Neuronal Ceroid Lipofuscinoses |
38. Zellweger Syndrome |
nice post. thanks.